Challenges with Gene Transfer Therapy in Neuromuscular Disease Summit – December 7, 2021
The Challenges with Gene Transfer Therapy in NMD Summit will explore questions and issues specific to gene transfer therapy in neuromuscular diseases through presentation and panel discussions. Topics of discussion will include dealing with pre-existing antibodies, re-dosing, efficiency and more.
Audiences for this summit include scientists, researchers and healthcare professionals who participate in gene therapy research, clinical trials and management of patients with NMD.* The title has been adjusted to more accurately recognize the evolution of the term per recent discussions and academic papers in the field.